The paper's citation list

No.
The paper's citation list
1
Development of Lanzyme as the Potential Enzyme Replacement Therapy Drug for Fabry Disease. 2022;13:53 doi: 10.3390/biom13010053
2
Cation-independent mannose 6-phosphate receptor: From roles and functions to targeted therapies. 2024;365:759 doi: 10.1016/j.jconrel.2023.12.014
3
Recent Therapeutic Advancements for Gaucher Disease. 2025;8: doi: 10.1002/adtp.202400292
4
Best Practices for Development and Validation of Enzymatic Activity Assays to Support Drug Development for Inborn Errors of Metabolism and Biomarker Assessment. 2024;26: doi: 10.1208/s12248-024-00966-y
5
Exploring the potential of bacterial-derived EVs for targeted enzyme replacement therapy: mechanisms, applications, and future directions. 2025;207: doi: 10.1007/s00203-025-04294-3
6
Targeting the Complement–Sphingolipid System in COVID-19 and Gaucher Diseases: Evidence for a New Treatment Strategy. 2022;23:14340 doi: 10.3390/ijms232214340
7
Investigation on Cross-correction of Cystinosis through Genetically Engineered Cells Secreting Cystinosin. 2024;13:46 doi: 10.2174/0122115501271925231130074832
8
Clinical Applications of Biomolecules in Disease Diagnosis. 2024;233 doi: 10.1007/978-981-97-4723-8_10
9
Targeted nanoliposomes to improve enzyme replacement therapy of Fabry disease. 2024;10: doi: 10.1126/sciadv.adq4738
10
From Molecular Therapies to Lysosomal Transplantation and Targeted Drug Strategies: Present Applications, Limitations, and Future Prospects of Lysosomal Medications. 2025;15:327 doi: 10.3390/biom15030327
11
Extracellular Vesicles as Tools for Crossing the Blood–Brain Barrier to Treat Lysosomal Storage Diseases. 2025;15:70 doi: 10.3390/life15010070
Rare Disease and Orphan Drugs Journal
ISSN 2771-2893 (Online)
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